Agalsidase beta treatment is associated with improved quality of life in patients with Fabry disease: findings from the Fabry Registry

Research output: Contribution to journalJournal articleResearchpeer-review

  • Watt, Torquil
  • Alessandro P Burlina
  • Chiara Cazzorla
  • Dorothee Schönfeld
  • Maryam Banikazemi
  • Robert J Hopkin
  • Ana Maria Martins
  • Katherine Sims
  • Dana Beitner-Johnson
  • Fanny O'Brien
  • Feldt-Rasmussen, Ulla
To evaluate the effect of agalsidase beta on longitudinal health-related quality of life in patients with Fabry disease.
Original languageEnglish
JournalJournal of Endodontics
Volume12
Issue number11
Pages (from-to)703-12
Number of pages10
ISSN0099-2399
DOIs
Publication statusPublished - 1 Nov 2010

ID: 34197994